"From our humble beginnings, we have provided a medical home for children and adults with rare genetic conditions. For over 30 years, we have stayed true to our mission of providing efficient and affordable healthcare to vulnerable individuals with genetic disease. We work tirelessly to advance effective treatment of genetic illnesses that would otherwise cause great suffering, through the integrations of genomic research and practical and affordable medical treatment."

During the past decade, Clinic for Special Children conducted 7 clinical trials. In the 10-year time frame, 7 clinical trials started and 1 clinical trials were completed, i.e. on average, 14.3% percent of trials that started reached the finish line to date. In the past 5 years, 4 clinical trials started and 1 clinical trials were completed. i.e. 25% of trials that started reached the finish line.

Out of the total clinical trials conducted in "Clinic for Special Children" #1 sponsor was "Audentes Therapeutics" with 2 trials, followed by "Novartis Gene Therapies" with 2 trials sponsored, "BioMarin Pharmaceutical" with 1 trials sponsored, "Clinic for Special Children" with 1 trials sponsored and "Illumina, Inc." with 1 trials sponsored. Other sponsors include -4 different institutions and companies that sponsored additional 6 trials in total.

In terms of collaborators to trials, out of the total clinical trials conducted in "Clinic for Special Children" #1 collaborator was "Genentech, Inc." with 1 trials as a collaborator, "Medical College of Wisconsin" with 1 trials as a collaborator and "PRA Health Sciences" with 1 trials as a collaborator. Other collaborators include -3 different institutions and companies that were collaborators in the rest 3 trials.

According to Clinical.Site data, the most researched conditions in "Clinic for Special Children" are "Crigler-Najjar Syndrome" (2 trials), "Genetic Disease" (2 trials), "Spinal Muscular Atrophy" (2 trials), "Phenylketonurias" (1 trials) and "SMA" (1 trials). Many other conditions were trialed in "Clinic for Special Children" in a lesser frequency.

Most popular intervention types in "Clinic for Special Children" are "Biological" (2 trials), "Drug" (1 trials) and "Genetic" (1 trials). Other intervention types were less common.

The name of intervention was led by "AT342" (1 trials), "Onasemnogene Abeparvovec-xioi" (1 trials), "Risdiplam" (1 trials) and "onasemnogene abeparvovec-xioi" (1 trials). Other intervention names were less common.

The vast majority of trials in "Clinic for Special Children" are 8 trials for "All" genders.

Currently, there are NaN active trials in "Clinic for Special Children". 1 are not yet recruiting, undefined are recruiting, 2 are Active, not recruiting, and undefined are Enrolling by invitation. In total, there were 4 completed trials in Clinic for Special Children, undefined suspended trials, and 1 terminated clinical trials to date.

Out of the total trials that were conducted in Clinic for Special Children, 1 "Phase 1" clinical trials were conducted, 0 "Phase 2" clinical trials and 2 "Phase 3" clinical trials were conducted as well. "Phase 4" trials included 1 trials, and there were also 0 trials that are defined as “Not Applicable".